Pluristem Reports Status of Orphan Drug Application for Aplastic Anemia
November 21 2012 - 5:00AM
Pluristem Therapeutics, Inc. (Nasdaq:PSTI)
(TASE:PLTR), a leading developer of placenta-based cell therapies,
today announced that the U.S. Food and Drug Administration (FDA)
has updated the Company on its application to designate Pluristem's
PLacental eXpanded (PLX) cells orphan drug status in the treatment
of aplastic anemia. The FDA acknowledged that aplastic anemia is a
rare disease with prevalence in the United States of less than
200,000. This serves as confirmation that aplastic anemia is an
indication for which candidate treatments are eligible for orphan
drug status. The FDA has also requested that Pluristem provide
additional information and data for further analysis before the FDA
can determine if the PLX cells can qualify for orphan drug
designation for aplastic anemia.
"We look forward to providing the additional information that
the FDA needs in connection with our orphan drug status application
for Aplastic Anemia. We appreciate the very productive working
relationship we have with the FDA, as we present PLX cells as
candidates for the treatment of a range of therapeutic
indications," stated Zami Aberman, Chairman and CEO of
Pluristem.
About Orphan Drug Status
Orphan drug designation qualifies a company for several benefits
under the Orphan Drug Act of 1983 (ODA), as amended. These benefits
include a 7-year period of orphan drug exclusivity upon product
approval, a tax credit for certain clinical testing expenses for
the orphan drug, written guidance on the non-clinical and clinical
studies needed to obtain marketing approval of an orphan drug, and
orphan drug grants.
About Pluristem Therapeutics Inc.
Pluristem Therapeutics Inc. (Nasdaq:PSTI) (TASE:PLTR) is a
leading developer of placenta-based cell therapies. The Company's
patented PLX (PLacental eXpanded) cells are a drug delivery
platform that releases a cocktail of therapeutic proteins in
response to a host of local and systemic inflammatory and ischemic
diseases. PLX cells are grown using the company's proprietary 3D
micro-environmental technology and are an "off-the-shelf" product
that requires no tissue matching prior to administration. Pluristem
is focusing on the use of PLX cells administered locally to treat
systemic diseases and potentially obviating the need to use the
intravenous route.
Pluristem has a strong patent portfolio, GMP certified
manufacturing and research facilities as well as strategic
relationships with major research institutions.
For more information visit www.pluristem.com, the content of
which is not part of this press release.
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Safe Harbor Statement
This press release contains forward-looking statements within
the meaning of the "safe harbor" provisions of the Private
Securities Litigation Reform Act of 1995 and federal securities
laws. For example, we are using forward looking statements when we
say that we look forward to providing the additional information
that the FDA needs, or when we discuss presenting our PLX cells as
candidates for treatment of a range of therapeutic indications.
These forward-looking statements are based on the current
expectations of the management of Pluristem only, and are subject
to a number of factors and uncertainties that could cause actual
results to differ materially from those described in the
forward-looking statements. The following factors, among others,
could cause actual results to differ materially from those
described in the forward-looking statements: changes in technology
and market requirements; we may encounter delays or obstacles in
launching our clinical trials; our technology may not be validated
as we progress further and our methods may not be accepted by the
scientific community; we may be unable to retain or attract key
employees whose knowledge is essential to the development of our
products; unforeseen scientific difficulties may develop with our
process; our products may wind up being more expensive than we
anticipate; results in the laboratory may not translate to equally
good results in real surgical settings; our patents may not be
sufficient; our products may harm recipients; changes in
legislation; inability to timely develop and introduce new
technologies, products and applications; loss of market share and
pressure on pricing resulting from competition, which could cause
the actual results or performance of Pluristem to differ materially
from those contemplated in such forward-looking statements. Except
as otherwise required by law, Pluristem undertakes no obligation to
publicly release any revisions to these forward-looking statements
to reflect events or circumstances after the date hereof or to
reflect the occurrence of unanticipated events. For a more detailed
description of the risks and uncertainties affecting Pluristem,
reference is made to Pluristem's reports filed from time to time
with the Securities and Exchange Commission.
CONTACT: Pluristem Therapeutics Inc.
William Prather R.Ph., M.D.
Sr. VP Corporate Development
1-303-883-4954
William.PratherMD@pluristem.com
Daya Lettvin
Director Investor & Media Relations
+972-54-674-5580
daya@pluristem.com